Tuesday, May 1, 2018

Therapeutic RNA corrects splicing defect that causes familial dysautonomia

Researchers have published a proof of concept for a therapeutic RNA drug to correct the error in RNA splicing that causes familial dysautonomia (FD), a rare inherited neurodegenerative disorder.

from Top Health News -- ScienceDaily https://ift.tt/2I1Nqys

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Scientists may have been wrong about what causes asthma

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