Thursday, July 6, 2023

Antisense therapy restores fragile X protein production in human cells

An antisense therapy restores production of the protein FMRP in cell samples taken from patients with fragile X syndrome. This breakthrough was possible because of the novel findings, also presented in the study, that aberrant alternative splicing of messenger RNA (mRNA) plays a principal role in fragile X syndrome, the most common form of inherited intellectual disability and the most frequent single-gene cause of autism.

from Top Health News -- ScienceDaily https://ift.tt/koNZVm3

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Scientists create “smart” DNA drug that targets cancer cells with extreme precision

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