Tuesday, May 1, 2018

Therapeutic RNA corrects splicing defect that causes familial dysautonomia

Researchers have published a proof of concept for a therapeutic RNA drug to correct the error in RNA splicing that causes familial dysautonomia (FD), a rare inherited neurodegenerative disorder.

from Top Health News -- ScienceDaily https://ift.tt/2I1Nqys

No comments:

Post a Comment

Florida housing market crumbles: Homeowners struggle to sell amid rising insurance costs and storm fears

from Yahoo News - Latest News & Headlines https://ift.tt/SqYdjcR